Get a closer look at the biotech ophthalmology landscape to discover exactly how companies are approaching the treatment of eye diseases.

The Rett Syndrome Research Trust (RSRT), the organization singularly focused on curing Rett syndrome, today announced 2025 research awards totaling $6.4 million, further advancing genetic medicine ...

Del-desiran reduced DMPK mRNA levels, but led to two serious adverse events ...

And the presence of the Barcelona Science Park, which is the first science park in Spain that is home to three research institutes and more than 70 companies, make the city a viable location for ...

A study using Ribo-STAMP technology reveals that protein production in brain cells varies significantly between different types of neurons, offering new insights into autism and memory.

Del-desiran effectively delivered siRNA to muscle, resulting in approximately 40% mean reduction in DMPK mRNA and amelioration of missplicingTreatment ...

Novo Nordisk advanced coramitug into the Phase III CLEOPATTRA trial, evaluating 1,280 patients with amyloid transthyretin cardiomyopathy or ATTR-CM. This decision was informed by results from their ...

Disc Medicine Inc (NASDAQ:IRON) operates in the healthcare sector, specifically within clinical stage biotechnology, a field known for long development timelines, strong reliance on clinical evidence, ...

UCLA researchers have developed a lipid nanoparticle-based gene-editing approach capable of inserting an entire healthy gene into human airway cells, restoring key biological function in a laboratory ...

A major breakthrough could help save the world’s bananas from a devastating disease. Scientists have discovered the exact ...

Crispr’s ability to cut genetic code like scissors has just started to turn into medicines. Now, gene editing pioneer ...

Cancer researchers are making strides in efforts to use genetic profiling to develop a more precise understanding of the ...